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Fabry disease: Difference between revisions
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<gallery>File:Morbus Fabry affected organs.svg.png</gallery> | <gallery>File:Morbus Fabry affected organs.svg.png</gallery> | ||
[[migalastat]] | [[migalastat]] received an orphan drug approval | ||
<ref>https://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/UCM616598.htm</ref> | <ref>https://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/UCM616598.htm</ref> | ||
<references/> | <references/> |
Revision as of 00:38, 11 August 2018
Fabry disease is a genetic condition involving lysosomal storage (E75.2)[1]
migalastat received an orphan drug approval [2]